Capricor Advances Deramiocel as FDA Review Continues
SAN DIEGO, August 13, 2026 Capricor Therapeutics continues to advance Deramiocel (CAP-1002) for Duchenne muscular dystrophy (DMD) as the...
rare diseases
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Cycle Pharmaceuticals Partners With Forma Life Sciences for CAVHANZA Supply
IRVINE, Calif., August 12, 2026 Cycle Pharmaceuticals announced a commercial manufacturing agreement with Forma Life Sciences to establish a...
PTC Therapeutics to Acquire ST-920 Fabry Gene Therapy Program
Warren, New Jersey, August 12, 2026 PTC Therapeutics announced that it was selected as the winning bidder to acquire...
Rhythm Pharmaceuticals Expands IMCIVREE Authorization in UK
Boston, Massachusetts, August 11, 2026 Rhythm Pharmaceuticals announced that the United Kingdom’s Medicines and Healthcare products Regulatory Agency (MHRA)...
Mereo BioPharma Advances Alvelestat Toward Phase 3 Trial
LONDON, UK; SOLANA BEACH, California; and AHMEDABAD, India, August 11, 2026 Mereo BioPharma Group plc and Sentynl Therapeutics, Inc.,...
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Bracco Gains FDA Clearance for VueJect Cardiac Imaging System
MILAN, Italy, August 11, 2026 Bracco Imaging has announced that its VueJect® ultrasound contrast delivery system has received 510(k)...
Alfasigma to Acquire Nordic Pharma in European M&A Deal
BOLOGNA AND MILAN, Italy, August 13, 2026 Alfasigma S.p.A. has entered into a share purchase agreement with SEVER Life...
EIT Pharma Gains FDA Acceptance for Lonafarnib NDA
Kirkland, Washington, August,11, 2026 EIT Pharma, Inc. has announced that the U.S. Food and Drug Administration (FDA) has accepted...
Vaderis Therapeutics Advances Engasertib Into Phase 3
Basel, Switzerland & Lincolnshire, Illinois, August,11, 2026 Vaderis Therapeutics, a clinical-stage biopharmaceutical company focused on targeted therapies for rare...
Jazz to Acquire Actio Biosciences for Rare Epilepsy Drug
Dublin, Ireland & San Diego, California, USA, August 10, 2026 Jazz Pharmaceuticals plc and Actio Biosciences, Inc. have announced...
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