FDA Expands Drug Repurposing Initiative for Rare Diseases
WASHINGTON, May 11, 2026 The U.S. Food and Drug Administration announced a new initiative aimed at accelerating drug repurposing...
rare diseases
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Santhera Pharmaceuticals Gains EU Boost for AGAMREE Expansion
PRATTELN, Switzerland, April 27, 2026 Santhera Pharmaceuticals has achieved a significant regulatory milestone with the European Medicines Agency’s (EMA)...
Novartis Itvisma Gains CHMP Boost for SMA Therapy
Basel, Switzerland | April 24, 2026 In a major breakthrough for rare disease treatment, Novartis has received a positive...
Polaryx Therapeutics Secures FDA Fast Track for PLX-200 in Rare Diseases
Paramus, New Jersey, USA, April 21, 2026 In a major regulatory advancement for rare disease therapeutics, Polaryx Therapeutics, Inc....
Immutep Secures FDA Orphan Status for Efti in Sarcoma
Sydney, Australia | April 15, 2026 Immutep Limited has achieved a significant regulatory milestone with the U.S. Food and...
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Jazz Pharmaceuticals Presents Neurology Drug Data at AAN
DUBLIN, Ireland, April 9, 2026 Jazz Pharmaceuticals plc has announced the presentation of six scientific abstracts, including one oral...
Immutrin Raises $87M to Advance Amyloidosis Antibody Therapy
CAMBRIDGE, UK, April 8, 2026 Immutrin Ltd has successfully raised £65 million ($87 million) in an oversubscribed Series A...
ALS Research at Risk from Proposed FY27 Budget Cuts
ARLINGTON, Virginia, United States, April 7, 2026 The ALS Association has issued a strong statement warning that the proposed...
Biogen to Acquire Apellis in $5.6B Strategic Pharma Deal
CAMBRIDGE, Mass. & WALTHAM, Mass., USA — March 31, 2026 In a major biopharmaceutical industry consolidation, Biogen Inc. has...
Recordati Confirms CVC Interest in Major Pharma M&A Deal
MILAN, Italy, March 26, 2026 Recordati S.p.A. has confirmed receiving a non-binding indication of interest from CVC Capital Partners...
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