MPS II

HYOGO, Japan, July 21, 2026 JCR Pharmaceuticals announced that the United Arab Emirates (UAE) has granted marketing authorization for...

SOUTH SAN FRANCISCO, Calif., June 18, 2026 Denali Therapeutics Inc. announced it has entered into a definitive agreement to...

HYOGO, Japan, June 8, 2026 JCR Pharmaceuticals Co., Ltd. announced new clinical findings from its J-Brain Cargo® blood-brain barrier...

SOUTH SAN FRANCISCO, Calif., March 25, 2026 In a landmark regulatory milestone, Denali Therapeutics announced that the U.S. Food...

EGENXBIO Inc. (Nasdaq: RGNX) announced positive 12-month pivotal data from its Phase I/II/III CAMPSIITE® trial of RGX-121 (clemidsogene lanparvovec),...