rare disease drug development

WALTHAM, Mass. — March 11, 2026 Pretzel Therapeutics announced new preclinical data for its lead therapeutic candidate PX578 during...

SAN FRANCISCO, March 3, 2026 Jaguar Health has secured an additional $3 million payment from Future Pak under a...

NOVATO, Calif., December 29, 2025 — Ultragenyx Pharmaceutical announced results from its Phase 3 Orbit and Cosmic clinical trials...